Sanofi Genzyme is currently looking for sites to participate in the feasibility for an upcoming Sanofi Genzyme study to assess a diagnostic protocol for individuals with unexplained splenomegaly and thrombocytopenia. This study will determine the prevalence of Gaucher Disease and Acid Sphingomyelinase Deficiency (Niemann-Pick A and B) among individuals with splenomegaly and thrombocytopenia who meet additional inclusion… read more //
Evaluating the effect of givosiran (ALN-AS1) on the rate of porphyria attacks in patients with Acute Hepatic Porphyrias (AHP). Trial Status: Enrolling Interested in learning more? Please email us at [email protected] For more info: ClinicalTrials.gov – NCT03338816
Cleveland Clinic Florida’s Maroone Cancer Center provides world-class care to patients with cancer and is at the forefront of new and emerging cancer research. Cleveland Clinic Florida’s cancer program is nationally recognized as High Performing by U.S. News & World Report 2017-18 “Best Hospitals” Miami-Fort Lauderdale metropolitan area ranking. By harnessing the benefits of advanced research and technology,… read more //
EmergingMed – Our clinical trial database includes all treatment trials from clinicaltrials.gov along with updates reported to us directly by trial sponsors and sites.
Florida Cancer Specialists & Research Institute (FCS) is committed to participating in the latest research, in order to find new and better treatments for patients. Their goal is to give patients access to the latest investigational therapies without having to travel long distances. FCS has 35 locations that directly participate in clinical trials. These sites… read more //
Transparency, integrity, and the patient are at the center of Takeda’s approach to clinical research.
Merck cares deeply about helping the world be well. We strive to improve health for others in the future by developing new drugs and vaccines that treat and prevent disease. Clinical trials are an essential part of this process. We are thankful for the thousands of volunteers — patients and healthy persons — who participate… read more //
At Bristol-Myers Squibb, our mission is to discover, develop, and deliver innovative medicines that help patients prevail over serious diseases. StudyConnect is the starting point for patients and caregivers, considering taking part in a clinical trial – a process to help make sure new medicines are effective and safe.
AmgenTrials.com is dedicated to bringing information about Amgen’s clinical trials to patients and healthcare communities. Patients looking for information about Amgen clinical trials can search the entire site using the condition, drug name, or protocol number.
Alexion Pharmaceuticals, Inc. is committed to research in rare diseases, and investigating potential new treatments that have the possibility of transforming patients’ lives.